FDA Expands Casgevy for Children 2+ with Sickle Cell Disease
The FDA approved the first gene therapy for children as young as 2 years old with sickle cell disease or transfusion-dependent beta thalassemia.
The FDA approved the first gene therapy for children as young as 2 years old with sickle cell disease or transfusion-dependent beta thalassemia.
A new class of drugs offers a disease-based approach to managing non-cystic fibrosis bronchiectasis by targeting airway inflammation.
The American Lung Association’s 2023 "State of Lung Cancer" report reveals improvement in five-year survival rate across the US, including for people of color.
New research suggests cystic fibrosis transmembrane conductance regulator (CFTR) modulators may provide mental health benefits for pediatric patients and their caregivers early in treatment.
The treatment combines two antibodies that attack the virus at different stages of infection, making it more difficult for the pathogens to develop resistance.
Remote monitoring did not increase the time spent at home after discharge among patients hospitalized with sepsis or lower respiratory tract infection, according to results from a randomized clinical trial of 1,286 adults.
The minimally invasive surgical approach may allow high-risk or frail patients to become candidates for lung transplantation.
The collaboration will focus on sleep and circadian medicine, including research into obstructive sleep apnea and wearable health technology.